National Tay-Sachs & Allied Diseases Association Receives U.S. Orphan Drug Designation for Novel Gene Therapy

Investigational Treatment for Tay-Sachs and Sandhoff Diseases in Phase 1 Planning

Boston, California, UNITED STATES


Investigational Treatment for Tay-Sachs and Sandhoff Diseases in Phase 1 Planning
BOSTON, June 13, 2013 (GLOBE NEWSWIRE) -- The U.S. Food and Drug Administration (FDA) has granted orphan drug designation to National Tay-Sachs and Allied Diseases Association (