Imbria_Logo_Colour.png
Imbria Pharmaceuticals to Present Results from IMPROVE-HCM Trial of Ninerafaxstat in Late-Breaking Clinical Trial Session at American College of Cardiology Annual Scientific Session & Expo (ACC.24)
25 mars 2024 08h00 HE | Imbria Pharmaceuticals Inc.
– Ninerafaxstat Phase 2 clinical trial in non-obstructive hypertrophic cardiomyopathy (nHCM) is complete;Phase 3 to be initiated in the 2H 2024 – BOSTON, March 25, 2024 (GLOBE NEWSWIRE) -- Imbria...
Catalyst Pharmaceutical logo
Catalyst Pharmaceuticals Announces AGAMREE® Now Commercially Available in the U.S. for the Treatment of Duchenne Muscular Dystrophy (DMD)
13 mars 2024 07h55 HE | Catalyst Pharmaceuticals, Inc.
AGAMREE® (vamorolone) a Novel Alternative Corticosteroid with Demonstrated Properties in Maintaining Efficacy and a Well-Tolerated Side Effect Profile Available in the U.S. by Prescription for...
logo.jpg
US Rare Disease Drug Market Drugs Sales Clinical Trials Insight
25 juil. 2023 03h12 HE | KuicK Research
Delhi, July 25, 2023 (GLOBE NEWSWIRE) -- US Orphan Drugs Market, Drugs Sales, Price, Dosage & Clinical Trials Insight 2028 Report Highlights: US Orphan Drugs Market Opportunity: > USD...
logo-01 (3) copy - Copy2.jpg
ConSynance Therapeutics Reports Positive Phase 1 Results for CSTI-500 in Prader-Willi Syndrome Patients
30 mai 2023 10h00 HE | ConSynance Therapeutics
RENSSELAER, New York, May 30, 2023 (GLOBE NEWSWIRE) -- ConSynance Therapeutics, Inc., an emerging biopharmaceutical firm focused on developing novel therapies for rare central nervous system (CNS)...
LOGO.jpg
QSAM Biosciences Receives Rare Pediatric Disease Designation from FDA for CycloSam in the Treatment of Osteosarcoma
02 févr. 2022 08h30 HE | QSAM Biosciences Inc.
Austin, TX, Feb. 02, 2022 (GLOBE NEWSWIRE) -- QSAM Biosciences Inc. (OTCQB: QSAM), a company developing next-generation therapeutic radiopharmaceuticals, including Samarium-153-DOTMP (CycloSam®),...
Follow one woman as she embarks on a journey of self-discovery in ‘The Royal Orphan’
11 mars 2021 01h39 HE | Archway Publishing
GRABILL, Ind., March 11, 2021 (GLOBE NEWSWIRE) -- An 18-year-old orphan comes to work for her kingdom’s royal family and soon finds romance, personal growth and tragedy in Lanelle Thomas’ new...
Equillium Logo.png
Equillium Granted U.S. FDA Orphan Drug Designations for EQ001 (itolizumab) for both the Prevention and Treatment of Acute Graft-Versus-Host Disease
07 févr. 2019 08h08 HE | Equillium
LA JOLLA, Calif., Feb. 07, 2019 (GLOBE NEWSWIRE) -- Equillium, Inc. (Nasdaq: EQ), a biotechnology company developing treatments for severe immuno-inflammatory disorders, today announced that the...
PledPharma applies f
PledPharma applies for an Orphan Drug Designation (ODD) in the US for Aladote
24 déc. 2018 02h00 HE | PledPharma AB
Stockholm, December 24, 2018. PledPharma AB (publ) announces that the company has filed an application for an Orphan Drug Designation (ODD) to the US FDA for the drug candidate Aladote®, developed to...
PledPharma har ansök
PledPharma har ansökt om särläkemedelsstatus (ODD) för Aladote i USA
24 déc. 2018 02h00 HE | PledPharma AB
Stockholm, 24 december 2018. PledPharma AB (publ) meddelar att bolaget har lämnat in en ansökan till amerikanska läkemedelsmyndigheten FDA om särläkemedelsstatus (ODD, Orphan Drug Designation) för...
Akari Logo (1).jpg
Akari Therapeutics Announces FDA Allowance of IND for Clinical Development of Coversin in PNH
03 janv. 2017 07h00 HE | Akari Therapeutics, Plc
NEW YORK and LONDON, Jan. 03, 2017 (GLOBE NEWSWIRE) -- Akari Therapeutics (NASDAQ:AKTX), an emerging growth, clinical-stage biopharmaceutical company, announced today that the U.S. Food and Drug...