Fairview Pharmacy Se
Fairview Pharmacy Service Receives URAC Rare Disease Designation
01 mars 2021 14h30 HE | URAC
Washington, DC, March 01, 2021 (GLOBE NEWSWIRE) -- Fairview Pharmacy Service Receives URAC Rare Disease Designation Among the first pharmacies in the country to achieve this mark of highest...
FIREFLY FUND HOSTS INAUGURAL RUN FOR RARE
28 févr. 2021 10h00 HE | Firefly Fund
Austin, Texas, Feb. 28, 2021 (GLOBE NEWSWIRE) -- To the 300 million people worldwide living with a rare disease, World Rare Disease Day, Feb. 28, is a time to shine a light on the life-altering...
Cat Lawyer Uses Vira
Cat Lawyer Uses Viral Internet Fame to Lend Nonprofit Support
25 févr. 2021 10h43 HE | Rod Ponton, Attorney at Law
Pecos, Texas, Feb. 25, 2021 (GLOBE NEWSWIRE) -- Rod Ponton, the Texas-based lawyer whose video went viral after he was stuck in a cat filter during an online call, is using his internet fame to...
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Children’s Mercy Kansas City Expands Investment in Pacific Biosciences Sequel IIe Systems to Scale Up Whole Genome Research Initiatives Focused on Rare Disease Diagnosis
24 févr. 2021 08h00 HE | Pacific Biosciences of California, Inc.
KANSAS CITY, Mo. and MENLO PARK, Calif., Feb. 24, 2021 (GLOBE NEWSWIRE) -- Pacific Biosciences of California, Inc. (Nasdaq: PACB), a leading provider of high-quality, long-read sequencing platforms,...
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European Commission Grants Ocugen Orphan Medicinal Product Designation for Gene Therapy Product Candidate, OCU400, For the Treatment of Both Retinitis Pigmentosa and Leber Congenital Amaurosis
23 févr. 2021 07h30 HE | Ocugen
MALVERN, Pa., Feb. 23, 2021 (GLOBE NEWSWIRE) -- Ocugen, Inc., (NASDAQ: OCGN), a biopharmaceutical company focused on discovering, developing, and commercializing gene therapies to cure blindness...
Saniona senarelägger
Saniona senarelägger publicering av bokslutskommuniké för 2020 till följd av omräkning och förnyad revision av tidigare finansiella rapporter för att uppfylla amerikanska revisionsstandarder
22 févr. 2021 17h59 HE | Saniona AB
PRESSMEDDELANDE 22 februari 2021 Saniona (OMX: SANION), ett biofarmaceutiskt företag med klinisk utveckling fokuserad på sällsynta sjukdomar, meddelar idag att bolaget, som ett led i den tidigare...
Saniona postpones 20
Saniona postpones 2020 year-end financial report due to restatement and re-audit of prior period financial statements in line with U.S. PCAOB audit standards
22 févr. 2021 17h59 HE | Saniona AB
PRESS RELEASE February 22, 2021 Saniona (OMX: SANION), a clinical stage biopharmaceutical company focused on rare diseases, today announced that, as part of its previously announced...
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Travere Therapeutics Announces Pricing of Public Offering of Common Stock
11 févr. 2021 22h03 HE | Travere Therapeutics, Inc.
SAN DIEGO, Feb. 11, 2021 (GLOBE NEWSWIRE) -- Travere Therapeutics, Inc. (Nasdaq: TVTX) today announced the pricing of an underwritten public offering of 6,550,000 shares of its common stock at a...
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Travere Therapeutics Announces Proposed Public Offering of Common Stock
10 févr. 2021 16h01 HE | Travere Therapeutics, Inc.
SAN DIEGO, Feb. 10, 2021 (GLOBE NEWSWIRE) -- Travere Therapeutics, Inc. (Nasdaq: TVTX) today announced that it intends to offer and sell, in an underwritten public offering and subject to market and...
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Inozyme Pharma Appoints Deborah Wenkert, M.D., as Senior Vice President and Chief Medical Officer
04 févr. 2021 06h00 HE | Inozyme Pharma Inc.
BOSTON, Feb. 04, 2021 (GLOBE NEWSWIRE) -- Inozyme Pharma, Inc. (Nasdaq: INZY), a clinical-stage biopharmaceutical company developing novel therapeutics for the treatment of rare diseases of abnormal...