National Tay-Sachs & Allied Diseases Association Receives U.S. Orphan Drug Designation for Novel Gene Therapy BOSTON, June 13, 2013 (GLOBE NEWSWIRE) -- The U.S. Food and Drug Administration (FDA) has granted orphan drug designation to National Tay-Sachs and Allied Diseases Association (NTSAD) for development...

Global Rare Disease Day NOVATO, CA--(Marketwire - February 23, 2009) - WHAT: Raptor Pharmaceuticals, San Francisco Bay Area biotech company, will participate in Global Rare Disease Day on February 28, 2009,...