Latest News and Press Releases

Agios provides update on Phase 2 trial of tebapivat in sickle cell disease

OMEICOS has successfully completed the End-of-Phase 2 (EOP2) meeting with the U.S. FDA enabling a pivotal study in Primary Mitochondrial Disease (PMD).

ROCKVILLE, Md., July 20, 2026 (GLOBE NEWSWIRE) -- Today, the American Kidney Fund (AKF) and the IgA Nephropathy Foundation announce the creation of a new resource for IgA nephropathy patients and...

ROCKVILLE, Md., July 20, 2026 (GLOBE NEWSWIRE) -- Today, the American Kidney Fund (AKF) and the IgA Nephrology Foundation announce the creation of a new resource for IgA nephropathy patients and...

Angelini Pharma Completes Acquisition of Catalyst Pharmaceuticals.

MELBOURNE, Australia, July 13, 2026 (GLOBE NEWSWIRE) -- CLINUVEL’s novel drug SCENESSE® (afamelanotide) has been granted a Notice of Compliance (NOC) by Health Canada for the prevention of...

Nonprofit Launches One of the Nation’s Most Comprehensive Education Resources for Inherited Retinal Diseases

Agios announces that the FDA has accepted its sNDA for mitapivat in sickle cell disease with a Priority Review

Phase 3 EPIDYS MRI data quantify givinostat’s potential to preserve functional muscle tissue and reduce fat infiltration in patients with Duchenne muscular dystrophy1Updated open-label extension data...

SERB Pharmaceuticals has completed the acquisition of development and commercialization rights to Idefirix (imlifidase) in Europe